2 Kids Suffering From Rare Disease Approved For Treatment - Philadelphia News, Weather and Sports from WTXF FOX 29

2 Kids Suffering From Rare Disease Admitted Into Gene Therapy Study

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Two kids who suffer from a rare disease that attacks the brain, nerves and muscles have been admitted into a gene therapy study that was considered to be their best hope.

FOX 29 introduced you to seven-year-old Eli and four-year-old Ella in October. The two, who are from the same family, were diagnosed with Metachromatic Leukodystrophy, also known as MLD.

A gene therapy study in Milan, Italy was their best chance.

On Friday, FOX 29 learned the two were admitted into the study. The family tells us their treatment is scheduled to begin in May.

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